PMC full text:
Lancet. Author manuscript; available in PMC 2018 Aug 26.
Published in final edited form as:
Lancet. 2017 Aug 26; 390(10097): 849–860.
Published online 2017 Jul 14. doi: 10.1016/S0140-6736(17)31868-8Figure 1
Phase 3 trial design
Visual field and a visual function questionnaire were additional, protocol-specified efficacy endpoints. vg=vector genomes. MLMT=multi-luminance mobility test. BCVA=best-corrected visual acuity. FST=full-field light sensitivity threshold.